FUCASO: Ko te Whakatairanga Tino-tangata BCMA CAR-T Therapy me te kaha me te haumaru kore e rite.
Ko te FUCASO, i whakawhanakehia e Nanjing IASO Biotechnology, he rongoa CAR-T hou i hangaia ki te whai i te antigen matuatanga pūtau-B (BCMA). Ko tenei rongoa e tu mai ana mo tana whaihua haumanu kore rite me tana tohu haumaru, e whakarato ana i te tumanako hou mo nga turoro me te mate mieloma maha (r/rMM) kua hoki mai. I whakaaetia e te National Medical Products Administration (NMPA) i te Pipiri 30, 2023, kua whakaatuhia e FUCASO te angitu nui i roto i nga tono haumanu.
Reiti Whakautu Nui: Kei te whakanui a FUCASO i te Reiti Whakautu Katoa (ORR) o 98.9% me te reeti Whakautu Katoa (CR) o 82.4%, tino teitei ake i etahi atu maimoatanga e waatea ana.
Te murunga roa: Ko nga turoro i tukinotia ki te FUCASO kua whakaatu i te 12-marama Progression-Free Survival (PFS) reiti o 85.5%, e tohu ana i te murunga mo te wa roa me te pai ake o te oranga.
Kōtaha Haumaru: Ki te ≥3 grade Cytokine Release Syndrome (CRS) e puta ana i roto i te 1% anake o nga turoro me te kore korero mo te ≥3 grade Immune Effector Cell-Associated Neurotoxicity Syndrome (ICANS), ka tukuna e FUCASO tetahi waahanga maimoatanga haumaru ake ki etahi atu maimoatanga CAR-T .
Utu-Painga: He iti ake te utu mo te maimoatanga FUCASO i nga rongoa rite e waatea ana i te United States, na te mea he whiringa pai mo te whānuitanga o nga turoro.
Tae Ao: Kua whakaturia e IASO BIO he whatunga pokapū maimoatanga matawhānui i Haina, e kaha ana ki te mahi i nga turoro mai i te ao katoa me nga ratonga whakauru mai i te whakawhitiwhiti korero ki te tiaki i muri i te maimoatanga.
Ko te manawanui tuatahi i rongoatia ki te FUCASO kua eke ki te rima tau o te oranga kore mate pukupuku, he tohu whakamiharo i whakaritea ki te tau waenga Progression-Free Survival (PFS) o te 2.9 marama noa me te tiaki paerewa. E whakaatu ana tenei i te kaha o FUCASO ki te huri i te whenua maimoatanga mo te mate myeloma maha.